We promise a united front.

Our management team has broad and deep expertise in rare disease drug development, particularly in lysosomal storage disorders (LSDs). We draw on deep, relevant experience in clinical development, regulatory affairs, manufacturing, commercial operations, financial management, and other key disciplines. We are passionate innovators who execute on our goals with discipline.

team

Cuong Do

Founder and Chairman

team

Eric Grinstead

Commercial

team

Bernadette Keane

CMC & Quality

team

Pawel Krysiak

President & CEO

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Lin Liu

Director, R&D

team

Gavin Malenfant

Portfolio