We are leading experts in lysosomal storage disorders.

Below please find a few of the most recent scientific publications developed by members of the M6P clinical development team:

• Engineering Of GlcNAc-1-Phosphotransferase For Production Of Highly Phosphorylated Lysosomal Enzymes For Enzyme Replacement Therapy.  Mol Ther Methods Clin Dev. 2017 Jun 16; 5: 59–65.

• A new platform technology for next generation lysosomal enzyme replacement and potential gene therapy in the treatment of lysosomal diseases. Poster session at WORLDSymposium, February 11, 2020.